Academic Journal

Combination HSCT and intravenous AAV-mediated gene therapy in a canine model proves pivotal for translation of Krabbe disease therapy

Bibliographic Details
Title: Combination HSCT and intravenous AAV-mediated gene therapy in a canine model proves pivotal for translation of Krabbe disease therapy
Authors: Bradbury, Allison M. 1, 2, 3, ∗, Bagel, Jessica 1, Swain, Gary 1, Miyadera, Keiko 1, Pesayco, Jill P. 4, Assenmacher, Charles-Antoine 5, Brisson, Becky 1, Hendricks, Ian 1, Wang, Xiao H. 6, Herbst, Zachary 7, Pyne, Nettie 2, Odonnell, Patricia 1, Shelton, G. Diane 4, Gelb, Michael 7, Hackett, Neil 8, Szabolcs, Paul 4, Vite, Charles H. 1, Escolar, Maria 6, 9
Source: In Molecular Therapy 3 January 2024 32(1):44-58
Database: ScienceDirect
Description
ISSN:15250016
DOI:10.1016/j.ymthe.2023.11.014