Academic Journal
O30: REKLAIM: A first in human phase Ib clinical trial of FBX-101 (AAVrh10.GALC) intravenously administered after UCBT for infantile Krabbe disease
| Τίτλος: | O30: REKLAIM: A first in human phase Ib clinical trial of FBX-101 (AAVrh10.GALC) intravenously administered after UCBT for infantile Krabbe disease |
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| Συγγραφείς: | Escolar, Maria, Lugt, Mark Vander, Wang, Raymond, Ruiz, Juan, Poe, Michele, Szabolcs, Paul |
| Πηγή: | Genetics in Medicine Open ; volume 2, page 100875 ; ISSN 2949-7744 |
| Στοιχεία εκδότη: | Elsevier BV |
| Έτος έκδοσης: | 2024 |
| Συλλογή: | ScienceDirect (Elsevier - Open Access Articles via Crossref) |
| Τύπος εγγράφου: | article in journal/newspaper |
| Γλώσσα: | English |
| DOI: | 10.1016/j.gimo.2024.100875 |
| Διαθεσιμότητα: | https://doi.org/10.1016/j.gimo.2024.100875 https://api.elsevier.com/content/article/PII:S2949774424000219?httpAccept=text/xml https://api.elsevier.com/content/article/PII:S2949774424000219?httpAccept=text/plain |
| Rights: | https://www.elsevier.com/tdm/userlicense/1.0/ ; https://www.elsevier.com/legal/tdmrep-license ; http://creativecommons.org/licenses/by-nc-nd/4.0/ |
| Αριθμός Καταχώρησης: | edsbas.F880D914 |
| Βάση Δεδομένων: | BASE |
| DOI: | 10.1016/j.gimo.2024.100875 |
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